This follows what appeared to be a generally positive data readout for belrestotug at ESMO 2024 just a few months ago.

Japan’s MHLW has approved Sarepta Therapeutics’ gene therapy Elevidys for treating Duchenne muscular dystrophy (DMD) ...

US President Donald Trump has signed an executive order telling drugmakers to cut prices to 'most favoured nation' pricing.

Orphan drug developers face significant difficulties when navigating market access frameworks in Europe. Could greater use of ...

Mobile healthcare, web-based tech, and wearables are all contributing to a clinical trials landscape that puts the patient ...

Abeona’s deal value is in line with recent voucher sale transactions amid uncertain times in rare disease drug development.

The European Commission (EC) has granted orphan drug designation to Biodexa Pharmaceuticals’ oral tablet formulation of ...

The Trump administration has introduced legislation outlining plans for deep cuts to Medicaid, possibly impacting millions of ...

GlobalData analysis predicts the global GLP-1RA market will reach $168bn by 2033, with Novo Nordisk and Eli Lilly to dominate ...

AI and machine learning can transform fragmented and unstructured healthcare data. But how do you refine it into useful, ...