Orphan drug developers face significant difficulties when navigating market access frameworks in Europe. Could greater use of ...

The FDA has cleared the IND for Ensoma's EN-374, targeting X-linked chronic granulomatous disease (X-CGD), a rare genetic ...

Mobile healthcare, web-based tech, and wearables are all contributing to a clinical trials landscape that puts the patient ...

Abeona’s deal value is in line with recent voucher sale transactions amid uncertain times in rare disease drug development.

US President Donald Trump has signed an executive order telling drugmakers to cut prices to 'most favoured nation' pricing.

The European Commission (EC) has granted orphan drug designation to Biodexa Pharmaceuticals’ oral tablet formulation of ...

The Trump administration has introduced legislation outlining plans for deep cuts to Medicaid, possibly impacting millions of ...

The UK MHRA has approved AstraZeneca's Trixeo Aerosphere inhaler to treat adults with chronic obstructive pulmonary disease ...

The Danish multinational said that Sogroya improved the yearly growth rate in pre-pubertal children born small for ...

The new site will support Roche and its unit Genentech's future portfolio of next-generation obesity medicines.

The executive order aims to cut US prescription drug costs by linking them to the lowest prices paid internationally.

Minghui Pharmaceutical has announced an exclusive licensing and partnership agreement with Qilu Pharmaceutical for MHB088C in ...