Children as young as five with severe inherited blood disorders will now be eligible for an innovative gene-editing treatment ...

What Is It, and Why Does It Matter? Casgevy (exagamglogene autotemcel) is a one-time gene therapy that uses a patient's own blood-forming stem cells. It helps people with certain medical conditions to ...

Transplants of blood-forming stem cells from umbilical cord blood may be an effective alternative to transplants of matched donor bone marrow stem cells to treat children with a rare, debilitating ...

Learn how gene editing is transforming sickle cell disease treatment and why expanding access to younger children matters. In a recent announcement, the U.S. Food and Drug Administration (FDA) ...

Discover nine of the best foods for sickle cell disease, including nutrient-rich options to support growth, immunity, and ...